BioOncology Watch

Timely Information for Practicing Physicians

 

august 2003

MULTIPLE MYELOMA (MM)

Bortezomib therapy of relapsed and refractory MM.  Bortezomib (Velcade; Millennium Pharmaceuticals), a novel proteasome inhibitor that promotes apoptosis through down-regulation of NF-kB, has demonstrated activity against MM in preclinical and phase I studies.  Paul Richardson et al report the results of a multicenter, single-arm trial in which 202 patients with relapsed MM that was also refractory to their most recent salvage therapy were administered bortezomib 1.3 mg/m2 intravenously twice weekly for 2 weeks every 3 weeks.  Oral dexamethasone (20 mg on the day of and the day after an infusion of bortezomib) was added at the time of disease progression or if the patient had stable disease after the first 4 cycles of single-agent bortezomib therapy.  The median number of prior antimyeloma therapies was 6 (range, 2-15) and 64% of patients had previously received a stem cell transplantation.  Among 193 patients with measurable disease, 27% of patients achieved at least a partial response (a ³50% reduction in myeloma paraprotein level) including 4% of patients with a complete response.  The median time to progression was 7 months (13 months for responders) and the median duration of response to single-agent bortezomib was 12 months (range, 1.3 to 16.7+ months).  The median overall survival was 16 months and according to a landmark analysis, responders to single-agent bortezomib had a longer survival than nonresponders (p = 0.007).  Thirteen (18%) of 74 patients receiving dexamethasone in addition to bortezomib had at least a minimal response (³25% reduction in myeloma paraprotein level).  Drug-related adverse events led to discontinuation of bortezomib in 36 (18%) patients and 12% of patients required at least one dose reduction.  The most common grade 3 and 4 toxicities included thrombocytopenia, neutropenia, neuropathy, and fatigue.  These data demonstrate that bortezomib is active in relapsed and refractory MM that is refractory to conventional chemotherapy.  (Richardson PG, et al. N Engl J Med 2003;348:2609-2617)

 

NON-SMALL CELL LUNG CARCINOMA (NSCLC)

Gefitinib therapy of recurrent or refractory NSCLC.  Gefitinib (Iressa; Astra Zeneca) is a selective epidermal growth factor receptor (EGFR) tyrosine kinase inhibitor that has shown activity against advanced NSCLC in early clinical trials.  The present study is a multicenter, randomized, double-blind phase II trial conducted by Masahiro Fukuoka and associates in which 210 patients with advanced NSCLC previously treated with 1 or 2 chemotherapy regimens (at least one containing platinum) received either 250-mg or 500-mg oral daily doses of gefitinib.  Objective tumor responses rates (18.4% [95% CI: 11.5-27.3%] and 19.0% [95% CI: 12.1-27.9%]), median progression-free survival times (2.7 and 2.8 months), and median overall survival times (7.6 and 8.0 months) were similar between the 2 treatment groups.  Symptom improvements, as measured by the Lung Cancer Subscale of the Functional Assessment of Cancer Therapy-Lung (FACT-L) quality-of-life instrument questionnaire, occurred in 69.2% and 85.7% of the 250 mg/day and 500 mg/day treatment groups, respectively.  Gefitinib-related toxicities were generally mild, but were more frequent in the patients treated with 500 mg/day.  Study withdrawal due to gefitinib toxicity was 1.9% and 9.4% for patients receiving gefitinib 250 and 500 mg/day, respectively.  These data showed that gefitinib therapy was active against NSCLC and provided symptom relief in patients with previously treated advanced NSCLC.  While efficacy between the 2 treatment groups was similar, the 250 mg/day dose had the more favorable safety profile.  The authors also noted an observation that warrants further investigation: adenocarcinoma is a prognostic factor that may be explained by the relatively slow growth of adenocarcinoma cells, thus potentially making them more sensitive to gefitinib.  (Fukuoka M, et al. J Clin Oncol 2003;21:2237-2246)

 

CHRONIC MYELOID LEUKEMIA (CML)

High-dose imatinib mesylate after failure of interferon-a.  Imatinib mesylate (Gleevec; Novartis Pharmaceuticals), a potent tyrosine kinase inhibitor with selectivity against c-abl and bcr/abl, has been shown to be effective against chronic-phase CML at doses of 400 mg daily.  The results of early clinical trials have suggested that imatinib dose escalation to 800 mg daily may improve results in selected patients.  In the current study, Jorge Cortes and others at the M. D. Anderson Cancer Center (Houston, TX) investigated whether higher doses of imatinib (400 mg twice daily) may be more effective in patients with chronic phase Philadelphia chromosome-positive CML after treatment failure with interferon-a.  Of 27 evaluable patients, 24 (89%) achieved a complete cytogenetic response.  Furthermore, quantitative polymerase chain reaction was performed in bone marrow from 32 patients and BCR-ABL was found to be undetectable in 13 patients (41%).  Toxicities were similar to those reported with standard-dose imatinib.  With a median follow-up of 15 months, all patients remained alive in chronic phase and 71% of patients continued to receive ³600 mg daily of imatinib.  These findings demonstrate that high-dose imatinib induces complete cytogenetic responses in most patients with chronic phase CML after interferon-a failure. The cytogenetic responses were associated with a high rate of molecular remission.  (Cortes J, et al. Blood 2003; 102: 83-86)

 

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